Cure Rare Disease (CRD) focuses on developing customized therapeutics for rare and ultra-rare neuromuscular diseases, particularly Duchenne muscular dystrophy (DMD) and other genetic disorders. They collaborate with top researchers, clinicians, and biotech partners to create personalized gene therapies for patients who have limited or no treatment options.
Key areas of support include:
Personalized Medicine Development – Designing custom gene therapies for individuals with unique genetic mutations.
Neuromuscular Diseases – Primarily focusing on Duchenne muscular dystrophy (DMD) and other related conditions.
Gene Editing & Drug Development – Utilizing CRISPR and other advanced technologies to create one-of-a-kind treatments.
Patient & Family Support – Working directly with affected families to provide hope and access to innovative therapies.
Scientific Research & Collaboration – Partnering with universities, medical institutions, and biotech companies to accelerate treatment discovery.
