Hello Everyone!
This year, I am raising money for a sweet friend of mine, William, who is 6 and fighting for a cure for Duchenne Muscular Dystrophy. His family is working with a team of amazing researchers at Cure Rare Disease who are developing life changing treatments for boys living with Duchenne.
These funds are going to fund the science behind customized gene therapies for William & others living with Duchenne. Why is custom important? Because in William’s case, there are no other boys living with his same mutation that we know of. Finding a solution for his mutation (duplication of exon’s 12-20) will treat him and him alone.
Duchenne Muscular Dystrophy is a muscle wasting disease that affects mostly boys. William is among about 250,000 boys living with this disease in the US today. There is no cure and it is 100% fatal. But…there is hope. Scientists are working hard to unlock a treatment that could prolong lives by decades using CRISPR technology. This is the research you are helping fund by donating today. There is hope for William and you can be a part of it.
Can you help me raise $ for his treatment this year?
Thank you!
Jaclyn
